Lysosomal and Rare Disorders Research and Treatment Center (LDRTC)
Non-profit OrganizationsVirginia, United States11-50 Employees
The Lysosomal and Rare Disorders Research and Treatment Center (LDRTC) is a non-profit organization based in Fairfax, Virginia, founded in 2013 by Dr. Ozlem Goker-Alpan, a recognized expert in lysosomal storage and other rare genetic disorders. The center pursues a translational, multidisciplinary approach that integrates basic and clinical research with patient care, aiming to improve diagnosis, treatment, and management of lysosomal and related diseases. Its work encompasses research to uncover disease mechanisms, identify biomarkers, and explore new therapeutic pathways, alongside education for patients, families, healthcare providers, and researchers. LDRTC emphasizes personalized medicine and flagship bench-to-bedside clinical protocols, including drug repurposing where appropriate, to address the needs of individuals affected by these rare disorders.