Zevra Therapeutics Email Format
Biotechnology ResearchMassachusetts, United States51-200 Employees
Zevra Therapeutics is a Boston-based biotechnology company with a commercial-stage profile and a late-stage pipeline focused on developing therapies for rare diseases. The company emphasizes collaboration with clinicians, patients, care partners, thought leaders, and advocacy groups in its clinical and regulatory development strategies. It relies on data-driven decision making and transparent narratives to navigate complex development challenges and advance therapies that could meaningfully benefit patients. It operates within the biotechnology research industry and aims to bring therapies to people living with rare diseases, engaging with a broad care ecosystem to inform development and access. In March 2026 Zevra announced a partnership with GeneDx to launch a sponsored genetic testing program for Niemann-Pick disease type C.