X4 Pharmaceuticals
Biotechnology ResearchMassachusetts, United States51-200 Employees
X4 Pharmaceuticals is a Boston-based biotechnology company focused on rare immune disorders. It operates as a fully integrated, commercial-stage organization that has brought XOLREMDI (mavorixafor) to the U.S. market for its first approved indication. The company is pursuing additional indications for mavorixafor and is conducting a global pivotal Phase 3 trial in chronic neutropenia. Its target market includes patients with rare hematologic or immune conditions and the clinicians who treat them, with a focus on meeting previously unmet therapeutic needs. The firm positions itself within the biotechnology industry as a specialized, commercially operating entity with ongoing development programs. In 2026, X4 Pharmaceuticals participated in the Jefferies Global Healthcare Conference.