Gene Therapy Program | University of Pennsylvania
Biotechnology ResearchPennsylvania, United States11-50 Employees
The Gene Therapy Program at the University of Pennsylvania is a biotechnology research initiative focused on discovering and translating gene therapy approaches, with an emphasis on developing next-generation gene transfer vectors and applying them to a range of inherited and acquired diseases. Led by Dr. James Wilson, the program has contributed to advancing gene transfer technology toward clinical use, evidenced by a substantial body of publications and patent activity. Located in Philadelphia, Pennsylvania, the program operates within the university's research ecosystem and has drawn support from a diverse mix of public and private sponsors. On October 1, 2024, the Gene Therapy Program transitioned its activities to Gemma Biotherapeutics (GEMMABio) and Franklin Biolabs. Its overarching objective is to develop and commercialize genetic-based therapeutics aimed at addressing the unmet needs of patients with inherited genetic diseases.